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Table 5 Characteristics of oldest child with Sanfilippo syndrome: interviews

From: Caregivers' assessment of meaningful and relevant clinical outcome assessments for Sanfilippo syndrome

  Median Range
Age (years) 9 (2–24)
  Count %
Sex   
 Male 10 53%
 Female 9 47%
Sub-type   
 A 13 68%
 B 5 26%
 C 1 5%
Staging   
 Early/mid stage 8 42%
 Later stage 11 58%
Participated in a clinical trial 6 32%
  1. n = 19