Skip to main content

Table 3 Characteristics of child with Sanfilippo syndrome: focus group survey (n = 10)

From: Caregivers' assessment of meaningful and relevant clinical outcome assessments for Sanfilippo syndrome

  Median Range
Age (years) 7.5 3–10
  Count % of respondents
Sex   
 Male 5 50%
 Female 5 50%
Sub-type   
 A 9 90%
 B 1 10%
Staging   
 Early/mid stage 7 70%
 Later stage 3 30%
Participated in a clinical trial 5 50%
  1. n = 11 (data missing from 1 participant)