Table 3 Characteristics of child with Sanfilippo syndrome: focus group survey (n = 10)
Median | Range | |
|---|---|---|
Age (years) | 7.5 | 3–10 |
Count | % of respondents | |
Sex | ||
Male | 5 | 50% |
Female | 5 | 50% |
Sub-type | ||
A | 9 | 90% |
B | 1 | 10% |
Staging | ||
Early/mid stage | 7 | 70% |
Later stage | 3 | 30% |
Participated in a clinical trial | 5 | 50% |