Societal perspectives on disease and treatment attributes characterizing rare diseases: a qualitative study from the United States

Journal of Patient-Reported Outcomes

Table 3 Attributes identified by respondents as important for DMD research and treatment (n = 30)

	n	%
Severity/impact on ADL/HRQoL	25	83.3
Limited lifespan	17	56.7
Young age at onset	15	50.0
Inherited/genetic/occurs in families	5	16.7
Lack of treatment availability/no cure presently	4	13.3
Impact on family/caregivers as well as patient	4	13.3
Rarity/disease prevalence	3	10.0

Attributes reported by a minimum of 10% of participants. Participants could specify more than one attribute as being important for research and treatment. Note only 30 participants responded to this set of questions, due to time constraints during the interview