Characteristic | Mean (SD) | Range |
---|---|---|
Age (years) | ||
Current | 11.5 (5.0) | 4–19 |
At diagnosis with nmDMD | 3.3 (1.0) | 1.8–4.8 |
Length of time on ataluren (years) | 4.4 (3.5) | 0.3–11 |
Current health state | N | |
Early ambulatory (age range 4–19 years) | 6 | |
Late ambulatory (age range 11–15 years) | 3 | |
Intermediate (aged 18 years) | 1 |