TY - JOUR AU - Lovley, Andrew AU - Raymond, Kimberly AU - Guthrie, Spencer D. AU - Pollock, Michael AU - Sanchorawala, Vaishali AU - White, Michelle K. PY - 2021 DA - 2021/01/07 TI - Patient-reported burden of hereditary transthyretin amyloidosis on functioning and well-being JO - Journal of Patient-Reported Outcomes SP - 3 VL - 5 IS - 1 AB - Hereditary transthyretin (hATTR) amyloidosis is a rare, systemic, progressive, and life-threatening disease in which transthyretin proteins misfold and aggregate as insoluble amyloid deposits, disrupting nervous, cardiac, gastrointestinal, and other organ tissues. There are limited available data about the experience of patients living with hATTR amyloidosis. This study used a qualitative, non-interventional design to explore the humanistic burden of hATTR amyloidosis from the patient’s perspective. SN - 2509-8020 UR - https://doi.org/10.1186/s41687-020-00273-y DO - 10.1186/s41687-020-00273-y ID - Lovley2021 ER -