Patients with worsening PS from baseline to safety follow-up (n = 50) | ||||
---|---|---|---|---|
Baseline Mean (SD) | Safety follow-up Mean (SD) | 95% CI | Effect Size | |
MDASI-MPM subscale | ||||
MDASI-MPM symptomsa | 2.2 (1.6) | 3.2 (1.9) | − 1.5 to − 0.5 | 0.69 |
MDASI-MPM interferencea | 2.8 (2.4) | 5.0 (2.8) | −3.0 to − 1.4 | 0.92 |
MDASI-MPM symptom | ||||
Trouble with balance or fallingb | 0.9 (1.6) | 2.7 (3.0) | 1.0 to 2.7 | 1.13 |
Eye problemsb | 0.5 (1.3) | 1.7 (2.2) | 0.4 to 1.8 | 0.92 |
Muscle weaknessb | 2.4 (2.6) | 4.5 (3.3) | 1.3 to 2.9 | 0.81 |
Numbnessb | 1.7 (2.7) | 3.7 (3.3) | 1.1 to 2.9 | 0.74 |
Dry mouthb | 1.7 (2.2) | 3.0 (2.4) | 0.5 to 2.1 | 0.59 |
Fatigue | 4.2 (2.5) | 5.4 (2.5) | 0.4 to 2.0 | 0.48 |
Feeling sad | 1.9 (2.6) | 3.1 (3.3) | 0.4 to 2.0 | 0.46 |
Feeling malaise | 2.5 (2.6) | 3.7 (3.0) | 0.2 to 2.2 | 0.46 |
Lack of appetite | 2.4 (2.7) | 3.5 (2.7) | 0.1 to 2.2 | 0.41 |
Distress | 2.4 (2.4) | 3.3 (3.0) | 0.1 to 1.6 | 0.38 |
Shortness of breath | 3.6 (2.4) | 4.5 (3.0) | −0.1 to 1.8 | 0.38 |
Chest heaviness | 2.2 (2.2) | 3.0 (2.9) | .01 to 1.5 | 0.36 |
Pain | 3.5 (2.7) | 4.3 (2.9) | −0.1 to 1.6 | 0.30 |
Feeling drowsy | 2.8 (2.7) | 3.5 (2.9) | −0.2 to 1.6 | 0.26 |
Coughing | 2.7 (2.8) | 2.0 (2.2) | −1.4 to 0.1 | 0.25 |
Difficulty remembering | 1.6 (2.1) | 2.1 (2.5) | −0.1 to 1.1 | 0.24 |
Disturbed sleep | 2.8 (2.9) | 3.2 (2.7) | −0.5 to 1.4 | 0.14 |
Nausea | 1.4 (1.9) | 1.2 (1.9) | −0.4 to 0.8 | 0.11 |
Vomiting | 0.7 (1.5) | 0.8 (1.3) | −0.3 to 0.6 | 0.07 |