Table 1 Demographics and clinical characteristics of participants at baseline
n = 63 | |
|---|---|
Mean (SD) participant age, years | 19.8 (6.1) |
Ambulatory status, n (%) | |
Early ambulatory | 11 (17.5) |
Late ambulatory | 8 (12.7) |
Non-ambulatory | 44 (69.8) |
Upper limb function, n (%) | |
Preserved | 18 (28.6) |
Mildly impaired | 22 (34.9) |
Moderately impaired | 18 (28.6) |
Loss of function | 5 (7.9) |
Ventilation use, n (%) | |
No ventilation | 30 (47.6) |
Nighttime ventilation | 24 (38.1) |
Daytime ventilation | 9 (14.3) |
Cardiomyopathy, n (%) | |
None/none identified | 28 (44.4) |
Asymptomatic | 26 (41.3) |
Symptomatic | 9 (14.3) |